Leading the Way on Rare & Serious Diseases

We are a global biotechnology leader focused on serving patients’ needs. Our scientists use the latest technologies to develop and deliver therapies that are used to treat rare and serious conditions, including immunodeficiency and autoimmune diseases, hereditary and acquired bleeding disorders, chronic inflammatory demyelinating polyneuropathy, hereditary angioedema, effects of enzyme deficiency on the lungs, as well as transplantation and critical care.